Dorota Gruber

Company: Cohen Children's Medical Center

Job title: Assistant Chief, Pediatric Cardiogenomics

Seminars:

Early Screening & Diagnosis of Neurological Disorders as a Means of Accelerating Gene Therapy Clinical Trials with Earlier Identification of Disease Benefits in Gene Therapy Clinical Trials: A Framework to Assess Disease-Modifying Therapies 11:30 am

Reviewing the status of the NBS for neurological disorders. Providing a framework for including neurological disorders in the NBS program. Examining lessons learned from NY NBS Duchenne pilot. Reviewing ethical, legal and social implications (ELSI) associated with early screening and diagnosis of late-onset neurological conditions.Read more

day: Clinical Stream Day 2 AM