Early Screening & Diagnosis of Neurological Disorders as a Means of Accelerating Gene Therapy Clinical Trials with Earlier Identification of Disease Benefits in Gene Therapy Clinical Trials: A Framework to Assess Disease-Modifying Therapies
Time: 11:30 am
day: Clinical Stream Day 2 AM
Details:
- Reviewing the status of the NBS for neurological disorders.
- Providing a framework for including neurological disorders in the NBS program. Examining lessons learned from NY NBS Duchenne pilot.
- Reviewing ethical, legal and social implications (ELSI) associated with early screening and diagnosis of late-onset neurological conditions.
