Sanjay Chandriani

Company: Maze Therapeutics

Job title: Director, Research and Development

Seminars:

Case Study: Highlighting Progress in a Gene Therapy Clinical Program for ALS 11:30 am

Outlining the study design for an ALS gene therapy program Delving into the successes and learnings from the trial so far Future expectations and hopes for progressionRead more

day: Clinical Stream Day 2 AM

Developing a Novel ATXN2-Targeting AAV Gene Therapy Treatment for Amyotrophic Lateral Sclerosis 11:30 am

Using human genetics, bioinformatics, and functional screens to identify a potent miRNA payload and an inert stuffer sequence Demonstrating preclinical efficacy in disease models of ALS Evaluating pharmacology, biodistribution in nonhuman primates in preparation for IND-enabling studiesRead more

day: Clinical Stream Day 1 AM