WORKSHOP B: Understanding Disease Biology to Aid your Target Validation & Gene Therapy Design
Time: 1:00 pm - 4:00 pm
day: DISCOVERY TRACK PM
Details:
Understanding the biology of your target disease is a hugely important consideration to implement at the very beginning of your development. This understanding will provide domino effects all the way to the clinic, particularly with more complex disease with multiple phenotypic expressions.
Join this workshop to learn:
- Ensuring a fundamental understanding of your target disease to aid in discovery and target identification
- Addressing Disease indications with multiple phenotype expressions and identifying which cell types to target
- Working with rare and ultra rare disorders with limited understandings of mechanisms of action
