Creating a Commercially Successful Product to Treat Rare Disorders
Time: 4:30 pm
day: Conference Day Two
Details:
- Exploring strategies and collaborations to ensure success of a therapy for rare and ultra rare disorders
- Discussing rare disease stakeholders: objectives, goals, accountability, transparency and communications
- Developing a roadmap for a successful product for ultra-rare disorders
- Cost breakdown for rare disorder’s gene therapies development – a case study
