Workshop A: Measuring Gene Therapy Success in the CNS

Tuesday, December 10 | 9:00am -12:00am

Monitoring the delivery success of gene therapies in the CNS can be challenging. The imaging techniques and gene expression analysis advances will be discussed.

By attending this workshop, you will:

  • Discuss gene therapy administration routes
  • Discover innovative imaging techniques for improving target engagement quantification
  • Evaluate current gene expression analysis techniques and the need for improvement in technology

Workshop Leader:


Eloise Hudry


Workshop B: Discovering Capsid Engineering Technology Advances

Tuesday, December 10 | 12:30pm - 3:30pm

Delivery is the greatest challenge for gene therapies targeting the CNS. Innovative vector technology is being developed to help improve the target engagement and cell specificity of gene therapy delivery.

Attend this workshop to:

  • Explore the use of vector engineering to improve gene therapy delivery
  • Discuss the promotors and regulators required for cell-specific expression
  • Debate the use of non-viral vs viral vectors

Workshop Leader:

david scaffer

David Schaffer
Professor of Chemical & Bimolecular Engineering & Director of the Berkeley Stem Cell Center
UC Berkeley
Co-Founder and Acting CSO
4D Molecular Therapeutics