Marie-Laure Nevoret

Marie-Laure Nevoret

Company: REGENXBIO

Job title: Senior Clinical Development Lead

Seminars:

Q&A Panel Discussion: Overcoming Toxicity & Immunogenicity Challenges 8:55 am

• Does it depend on the disorder? • What are best preclinical models for toxicology risk assessment? • Reviewing preclinical data for CNS and systemic toxicity • How does this translate into humans? • Discussing immunogenicity concerns for patientsRead more

day: Day Two

Intracisternal AAV9-based Gene Therapy for Lysosomal Storage Diseases: The Clinical Trial Experience 8:35 am

• Intracisternal route of administration in pediatric MPS I and II patients • Safety and monitoring of intracisternal AAV9 gene therapy • Biomarker and clinical outcomes assessment challenges in heterogenous phenotypes of MPS II • Progress and update of the first in human AAV9 gene therapy studies for MPS I and IIRead more

day: Day Two

© Copyright 2018 Hanson Wade | Design and site by Event Engine | Hanson Wade Limited is registered in England & Wales, number 06752216.
Registered Office: Suite A, 6 Honduras Street, London EC1Y 0TH.