Lisa Spronck

Lisa Spronck

Company: UniQure

Job title: Non-Clinical Development Scientist

Seminars:

First-in-Human AAV Gene Therapy for Huntington’s Disease – from Pre-Clinical to the Clinic 8:55 am

AAV5-miRNA gene therapy as potential treatment for Huntington’s disease miRNA mediated huntingtin lowering in small and large animal models for Huntington’s disease MRI guided intra-striatal administration of AAV5-miTT in large animals to investigate safety, biodistribution and efficacy in support of a clinical trialRead more

day: Day Two

Q&A Panel Discussion: Overcoming Toxicity & Immunogenicity Challenges 9:25 am

• Does it depend on the disorder? • What are best preclinical models for toxicology risk assessment? • Reviewing preclinical data for CNS and systemic toxicity • How does this translate into humans? • Discussing immunogenicity concerns for patientsRead more

day: Day Two

© Copyright 2018 Hanson Wade | Design and site by Event Engine | Hanson Wade Limited is registered in England & Wales, number 06752216.
Registered Office: Suite A, 6 Honduras Street, London EC1Y 0TH.