PANEL: How Do We Know Our Therapy Works?

Time: 12:00 pm
day: Day One: Track A AM


  • Assessing the preclinical development of biomarkers to demonstrate efficacy and aid clinical translation
  • What are key hurdles prohibiting effective assessments of preclinical efficacy for CNS targeted gene therapies and how can biomarkers be leveraged to tackle such challenges?
  • How can we leverage technological innovation within the digital biomarkers field to better determine therapeutic response?