2019 Full Event Guide

GTXN Brochure

18+ industry experts will present their latest research on the hottest topics in gene therapy for neurological disorders, including:

  • The pros and cons of different gene therapy administration routes for more efficient delivery
  • Addressing immunogenicity and dosage challenges without compromising efficacy
  • Introducing novel capsids and advances in capsid engineering for improved cell targeting
  • Improving transduction efficiency and exploring advances in technology for monitoring gene expression
  • Accounting for limited large mammal model availability and accounting for limitations for improved translation
  • Discuss the future of CRISPR and gene editing for CNS disorders to assess different genetic therapeutic approaches